Genethon researchers have made significant progress in developing a novel approach to designing gene therapy vectors using artificial intelligence (AI). A study published in Nature Communications details their work on perfecting an innovative methodology for creating new capsids, which are the protein shells that encase genetic material in gene therapy treatments. This breakthrough has potential applications in treating muscle diseases, according to the research.
https://www.businesswire.com/news/home/20241219420964/en/A-Phase-3-Ready-DMD-Gene-Therapy-a-Clinical-Trial-to-Offset-AAV-Neutralizing-Antibodies-and-an-AI-Inspired-New-Generation-of-Capsids-Highlight-Genethon%E2%80%99s-2024-Fall-Milestones